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Company Information:

Name: REGENX BIOSCIENCES, LLC
Address: 750 17TH ST NW, STE 1100
WASHINGTON, DC 20006-
Located in HUBZone: No
Woman-Owned: No
Minority-Owned: No
URL: N/A
Phone: N/A

Award Totals:

Program/Phase Award Amount ($) Number of Awards
SBIR Phase I $829,025.00 3
STTR Phase I $211,009.00 1

Award List:

Scalable Production of New Generation Adeno-Associated Virus Gene Therapy Vectors

Award Year / Program / Phase: 2010 / SBIR / Phase I
Agency: HHS
Principal Investigator: Karen Kozarsky
Award Amount: $263,277.00
Abstract:
DESCRIPTION (provided by applicant): The overall goal of this application is to develop a scalable production system for the manufacture of an adeno- associated virus (AAV) serotype 8-based gene therapy vector bearing a human low density lipoprotein recept or (hLDLR) transgene for the treatment of… More

AAV Mediated Gene Transfer to the CNS for MPS I

Award Year / Program / Phase: 2012 / STTR / Phase I
Agency: HHS
Research Institution: UNIVERSITY OF MINNESOTA
Principal Investigator: Karen Kozarsky – 202-577-4374
Award Amount: $211,009.00
RI Contact:
Abstract:
DESCRIPTION (provided by applicant): Mucopolysaccharidosis type I (MPS I) is an autosomal recessive storage disease caused by the absence of a-L-iduronidase (IDUA), resulting in systemic accumulation of glycosaminoglycan (GAG) storage materials, hepatosplenomegaly, skeletal dysplasias,… More

Novel Adeno-Associated Viral Therapy for Wet Age-Related Macular Degeneration

Award Year / Program / Phase: 2012 / SBIR / Phase I
Agency: HHS
Principal Investigator: Karen Kozarsky – 202-577-4374
Award Amount: $304,421.00
Abstract:
DESCRIPTION (provided by applicant): The overall goal of this project is to develop a novel gene-based delivery system to treat neovascular age- related macular degeneration (wet AMD), a debilitating ocular disease. AMD is the leading cause of blindness inAmericans over 60 years of age, with wet AMD… More

Genetically-delivered Bevacizumab for Treatment of Wet Age-Related Macular Degene

Award Year / Program / Phase: 2013 / SBIR / Phase I
Agency: HHS
Principal Investigator: Karen Kozarsky – 202-577-4374
Award Amount: $261,327.00
Abstract:
DESCRIPTION (provided by applicant): The goal of this Phase I SBIR is the pre-clinical development of a novel gene-based delivery system for bevacizumab (anti-VEGF antibody) to treat wet age-related macular degeneration (AMD). The premise is based on: (1)the demonstrated efficacy of monthly… More